“I’d go on a hike with my kids… that would make me feel so happy.” Recognising what people with haemophilia B identify as meaningful when considering personal goals and the potential for gene therapy
Khair, Kate, Nagra, Ranjit, Gorman, Richard, Fletcher, Simon, Jenner, Kathryn, Trim, Joe, Collings, Shuk-Li
The journey of gene therapy in haemophilia – putting the patient at the centre of the hub and spoke model
Noone, Declan, Astermark, Jan, O'Mahony, Brian, Peyvandi, Flora, Khair, Kate, Pembroke, Luke, Jenner, Kathryn
Shared decision-making for gene therapy in haemophilia care
Fletcher, Simon, Jenner, Kathryn, Khair, Kate