Gene therapy for inherited metabolic diseases

Authors

Genetics and Genomic Medicine, Great Ormond Street Institute of Child Health, University College London, London, UK

Department of Paediatric Metabolic Medicine, Faculty of Medicine, Mersin University, Mersin, Turkey

Genetics and Genomic Medicine, Great Ormond Street Institute of Child Health, University College London, London, UK

Genetics and Genomic Medicine, Great Ormond Street Institute of Child Health, University College London, London, UK

Developmental Neurosciences Research and Teaching Department, Great Ormond Street Institute of Child Health, University College London, London, UK

National Institute of Health Research, Great Ormond Street Hospital Biomedical Research Centre, London, UK

Genetics and Genomic Medicine, Great Ormond Street Institute of Child Health, University College London, London, UK

Metabolic Medicine Department, Great Ormond Street Hospital for Children, NHS Foundation Trust, London, UK

National Institute of Health Research, Great Ormond Street Hospital Biomedical Research Centre, London, UK