Have a personal or library account? Click to login
Post-radiation xerostomia therapy with allogeneic mesenchymal stromal stem cells in patients with head and neck cancer: study protocol for phase I clinical trial Cover

Post-radiation xerostomia therapy with allogeneic mesenchymal stromal stem cells in patients with head and neck cancer: study protocol for phase I clinical trial

Open Access
|Nov 2023

Figures & Tables

FIGURE 1.

Design of the clinical trial.CTCAE v5 = Common Terminology Criteria for Adverse Events version 5.0; MRI = magnetic resonance imaging; MSC = allogeneic mesenchymal stromal stem cells; RT = radiotherapy; SCC = squamous cell carcinoma; US = ultrasound; [99mTc]HMPAO = Technetium 99m-hexamethylpropyleneamine oxime; [99mTc]TcO4 = Technetium 99m-pertechnetate
Design of the clinical trial.CTCAE v5 = Common Terminology Criteria for Adverse Events version 5.0; MRI = magnetic resonance imaging; MSC = allogeneic mesenchymal stromal stem cells; RT = radiotherapy; SCC = squamous cell carcinoma; US = ultrasound; [99mTc]HMPAO = Technetium 99m-hexamethylpropyleneamine oxime; [99mTc]TcO4 = Technetium 99m-pertechnetate

Inclusion and exclusion criteria

Inclusion criteriaExclusion criteria
Squamous cell carcinoma of the oropharynx, UICC TNM (8th ed.) stage cT1–2N+ or cT3–4cN0–3 M0, treated with curative intent RT (TD 66–70 Gy, bilateral neck irradiation) with or without concurrent chemotherapyNewly diagnosed malignant tumor anywhere in the body within the last two years
Two years or more after treatment with no evidence of locoregional recurrence or systemic metastasisActive smoker
Nonsmoker or former smoker (quit smoking ≥ 2 years ago)Use of xerogenic medications (e.g., tricyclic antidepressants, antipsychotics, decongestants, bronchodilators, antihypertensive agents such as beta blockers and diuretics, antihistamines, hypnotic sedatives, opioids, and muscle relaxants)
Mean radiation dose > 26 Gy to each of the parotid glands and > 35 Gy to each of the submandibular glandsOther salivary gland disorders (e.g., Sjoegren's syndrome, scleroderma, sialolithiasis, etc.)
Grade 2 or 3 xerostomia as assessed by the CTCAE v5.0 scalePatients receiving anticoagulant therapy that cannot be discontinued during the procedure
Clinically decreased salivation and hyposalivation (unstimulated total salivary flow of 0.05–0.20 ml/min)Pregnancy or planned pregnancy within the next two years
Age between 18–75 yearsBreastfeeding
Both sexesActive, uncontrolled infection
Signed “Informed Consent Form” to participate in the studyOther medical (including psychiatric) conditions that, in the opinion of the investigators, preclude safe administration of the planned therapy and completion of follow-up visits
Known substance abuse or alcoholism

Procedures of the study

ProceduresInclusionInterventionFollow-up examinations

W4→0D0D1D5D28D120
Patient screening with clinical and objective evaluation of xerostomia1X
Complete blood count, biochemistryX XX
Coagulation profileX
Measurement of unstimulated and stimulated salivary flow rateX XX
Determination of salivary compositionX XX
Magnetic resonance imagingX XX
US elastographyX XX
Scintigraphy with [99mTc]Tc-HMPAO labeled MSCs X
Scintigraphy with ([99mTc]TcO4)X X
Core needle biopsy of the gland2X X
Visual Analog Scale questionnaireX XX
Xerostomia QuestionnaireX XX
EORTC QLQ-H&N35X XX
Toxicity assessment, CTCAE v.5 XXXXX

Primary and secondary objectives of the study

ObjectiveDefinition of objectiveTime of evaluation
Primary
  Evaluation of the safety of administration of allogeneic MSCsAdverse event assessment (CTCAE v.5 criteria): pain at application site, mouth sensation, infectionFrom the start of therapy to the last follow-up (days 1, 5, 28, and 120)
Secondary
  Efficacy of the procedureMeasurement of unstimulated/stimulated salivary flow and saliva compositionDuring recruitment, day 28 and 120 post-procedure
Assessment of subjective degree of xerostomia (questionnaires)During recruitment, days 28 and 120 after the procedure
Immediately after the procedure (day 0)
Scintigraphic evaluation of grafting, retention, and migration of allogeneic MSCsDuring recruitment, on days 28 and 120 after the procedure
Assessment of patients’ quality of life
  Radiological changes of the salivary tissueMagnetic resonance imaging (MRI): volume, signal, and diffusivity changesDuring recruitment, on days 28 and 120 after procedure
Ultrasonography (US): consistency (firmness)
  Functional changes of the salivary tissueScintigraphy with ([99mTc]TcO4 (pertechnetate): uptake of radioisotope in parenchyma, ejection fractionDuring recruitment, on days 28 and 120 after procedure
  Morphological changes of the salivary tissueCore needle biopsy specimens: composition, inflammatory infiltrate, metaplasia, reactive changesDuring recruitment, on day 120 after the procedure
DOI: https://doi.org/10.2478/raon-2023-0052 | Journal eISSN: 1581-3207 | Journal ISSN: 1318-2099
Language: English
Page range: 538 - 549
Submitted on: Sep 4, 2023
Accepted on: Sep 25, 2023
Published on: Nov 30, 2023
Published by: Association of Radiology and Oncology
In partnership with: Paradigm Publishing Services
Publication frequency: 4 issues per year

© 2023 Primoz Strojan, Gaber Plavc, Marko Kokalj, Goran Mitrovic, Olga Blatnik, Luka Lezaic, Aljaz Socan, Aljosa Bavec, Natasa Tesic, Katrina Hartman, Urban Svajger, published by Association of Radiology and Oncology
This work is licensed under the Creative Commons Attribution 4.0 License.