Abstract
Investigators from Europe and the USA, representing the STRIDE Registry and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS), examined the effectiveness of ataluren and standard of care in the Registry versus stand of care alone in the CINRG DNHS.
DOI: https://doi.org/10.15844/pedneurbriefs-34-12 | Journal eISSN: 2166-6482
Language: English
Page range: 12 - 12
Submitted on: Mar 6, 2020
Accepted on: Nov 29, 2020
Published on: Dec 4, 2020
Published by: Pediatric Neurology Briefs Publishers
In partnership with: Paradigm Publishing Services
© 2020 Sameh S. Morkous, published by Pediatric Neurology Briefs Publishers
This work is licensed under the Creative Commons Attribution 4.0 License.